Tag Archives: patients

FDA Approves Nulibry (fosdenopterin) to Reduce the Risk of Mortality in Patients with Molybdenum Cofactor Deficiency (MoCD) Type A

FDA Approves Nulibry (fosdenopterin) to Reduce the Risk of Mortality in Patients with Molybdenum Cofactor Deficiency (MoCD) Type A PALO ALTO, February 28, 2021 – BridgeBio Pharma, Inc. (Nasdaq: BBIO) (BridgeBio) and affiliate Origin Biosciences, Inc. (Origin) today announced the U.S. Food and Drug Administration (FDA) has approved Nulibry (fosdenopterin) for Injection as the first… Read More »

FDA Approves Amondys 45 (casimersen) Injection for the Treatment of Duchenne Muscular Dystrophy (DMD) in Patients Amenable to Skipping Exon 45

FDA Approves Amondys 45 (casimersen) Injection for the Treatment of Duchenne Muscular Dystrophy (DMD) in Patients Amenable to Skipping Exon 45 CAMBRIDGE, Mass., Feb. 25, 2021 (GLOBE NEWSWIRE) —  Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced that the U.S. Food and Drug Administration (FDA) has approved Amondys… Read More »

Repeal of Obamacare Could Leave Young Cancer Patients in the Lurch

THURSDAY, Oct. 22, 2020 — If Obamacare, or the Affordable Care Act (ACA), is repealed, pediatric cancer patients could lose critical insurance coverage, a new study warns. Kids with cancer often require intensive treatment and long-term follow-up to beat the disease. The ACA allows them to stay on their parents’ insurance coverage to age 26… Read More »

A patient’s COVID-19 reflections

In this age of the coronavirus pandemic, every moment of life takes on new meaning and importance. Decisions must be made based upon facts known, not assumed. Everything requires careful thought and planning, like a trip to the pharmacy for refills of prescriptions or a trip to the local grocery store to pick up needed… Read More »